Top

News

01.03.21

QualityMetric Collaborates with Drug Developers to Address Pain Points of Rare Diseases

QualityMetric collaborates with drug developers to address pain points of rare diseases

We offer several patient-reported outcome (PRO) measurement solutions that can help document the etiology, progression, patient experience, symptoms and impact of rare diseases.

 

On rare disease research

Drug developers face many unique challenges in developing rare disease treatments: natural history is often poorly understood and characterized, diseases tend to be life-limiting, small populations restrict study design and replication. They’re also challenged by the lack of validated tools to assess outcomes. 

 

QualityMetric offers several patient-reported outcome (PRO) measurement solutions that can help developers of drugs for rare diseases address these pain points. Our solutions can help document the etiology, progression, patient experience, symptoms and impact of rare diseases.

 

Our disease-specific surveys allow you to engage meaningfully with patient advocacy groups for recruitment and help gather critical information about the patient experience and unmet need for treatment, and inform the selection of endpoints for efficacy trials.

 

QualityMetric’s PRO solutions can help you meet FDA recommendations to document the natural history of rare diseases via qualitative research studies.